Lysosomal Storage Disease Market: How Is Gene Therapy Transforming the LSD Treatment Landscape?
Gene therapy's LSD treatment landscape transformation — the clinical advancement of gene therapy approaches for lysosomal storage diseases — where viral vector delivery of functional lysosomal enzyme genes (adeno-associated virus, lentiviral vectors) or genome editing approaches (CRISPR-Cas9) enable one-time or durable treatment that could fundamentally displace the chronic enzyme...
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